CHARACTERIZING PROGRESSIVE DISEASE BURDEN AMID HETEROGENEITY: DATA VISUALIZATIONS FOR AMBULATORY MOTOR FUNCTION IN DUCHENNE MUSCULAR DYSTROPHY (DMD)

被引：0
|
作者：
Mayhew, A. [1 ]
Signorovitch, J. [2 ]
Johnson, M. [2 ]
Frean, M. [2 ]
Ward, S. J. [3 ]
Posner, N. [4 ]
Merla, V [4 ]
Mahn, M. [4 ]
Stimpson, G. [5 ]
Guglieri, M. [6 ]
Straub, V [1 ]
Lofra, Muni R. [1 ]
Manzur, A. [7 ,8 ]
Baranello, G. [9 ]
Muntoni, F. [10 ]
机构：
[1] John Walton Muscular Dystrophy Res Ctr, London, England
[2] Anal Grp Inc, Boston, MA USA
[3] Collaborat Trajectory Anal Project cTAP, Cambridge, MA USA
[4] Pfizer Inc, New York, NY USA
[5] Dubowitz Neuromuscular Ctr, London, England
[6] Univ Newcastle, Newcastle Upon Tyne, Tyne & Wear, England
[7] UCL, Great Ormond St Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
[8] Great Ormond St Hosp Sick Children, London, England
[9] Dubowitz Neuromuscular Ctr, London, England
[10] UCL, London, England
来源：
VALUE IN HEALTH | 2023年 / 26卷 / 06期
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中图分类号：
F [经济];
学科分类号：
02 ;
摘要：
PCR174
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页码：S344 / S344
页数：1
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