共 50 条
- [2] Clinical trials and rare diseases NEW ENGLAND JOURNAL OF MEDICINE, 2003, 348 (24): : 2455 - 2456
- [4] Methodology of clinical trials for rare diseases BEST PRACTICE & RESEARCH IN CLINICAL RHEUMATOLOGY, 2014, 28 (02): : 247 - 262
- [10] Room for improvement in clinical trials for rare diseases Nature Reviews Rheumatology, 2020, 16 : 131 - 132