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- [1] Magnetic resonance imaging findings and novel mutations in GM1 gangliosidosisJOURNAL OF CHILD NEUROLOGY, 2005, 20 (01) : 57 - 60Gururaj, A论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesSztriha, L论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesHertecant, J论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesJohansen, JG论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesGeorgiou, T论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesCampos, Y论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab EmiratesDrousiotou, A论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab Emiratesd'Azzo, A论文数: 0 引用数: 0 h-index: 0机构: United Arab Emirates Univ, Fac Med, Dept Paediat, Al Ain, U Arab Emirates
- [2] GENE-THERAPY IN GM1 GANGLIOSIDOSISFASEB JOURNAL, 1994, 8 (07): : A1440 - A1440SEO, HC论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USAJOHNSON, PA论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USAPYRCE, D论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USAMASADA, RI论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USAKISHIMOTO, Y论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USAOBRIEN, JS论文数: 0 引用数: 0 h-index: 0机构: GLYKO INC, NOVATO, CA 94949 USA
- [3] Intravenous Delivery of AAV Gene Therapy in GM1 GangliosidosisMOLECULAR THERAPY, 2018, 26 (05) : 136 - 136Gross, Amanda L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAGray-Edwards, Heather论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA论文数: 引用数: h-index:机构:Maitland, Stacy论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA
- [4] Intravenous Delivery of AAV Gene Therapy in GM1 GangliosidosisMOLECULAR THERAPY, 2019, 27 (04) : 191 - 191Gross, Amanda L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAGray-Edwards, Heather L.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Radiol, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USABebout, Cassie N.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USANeilson, Kayly论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USABrunson, Brandon L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA论文数: 引用数: h-index:机构:Maitland, Stacy论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Radiol, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMartin, Douglas论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA
- [5] Intravenous Delivery of AAV Gene Therapy in GM1 GangliosidosisMOLECULAR THERAPY, 2017, 25 (05) : 315 - 315Gross, Amanda L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAGray-Edwards, Heather论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Dept Neurol & Gene Therapy Ctr, Media Sch, Worcester, MA 01605 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA
- [6] Presymptomatic Gene Therapy Cures Feline GM1 GangliosidosisMOLECULAR THERAPY, 2012, 20 : S12 - S12McCurdy, Victoria J.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAJohnson, Aime K.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USABradbury, Allison M.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USARandle, Ashley N.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAGray-Edwards, Heather论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAHwang, Misako论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USALeroy, Stanley G.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USACox, Nancy R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA
- [7] Developement of an Ex Vivo Gene Therapy for Infantile GM1 GangliosidosisMOLECULAR THERAPY, 2023, 31 (04) : 38 - 39Bucciarelli, Linda论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, Italy Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, ItalyFabris, Camilla论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, Italy Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, ItalyMilazzo, Rita论文数: 0 引用数: 0 h-index: 0机构: Altheia Sci Srl, Milan, Italy Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, ItalyBiffi, Alessandra论文数: 0 引用数: 0 h-index: 0机构: DFCI BCH Canc & Blood Disorders Ctr, Boston, MA USA Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, ItalyPoletti, Valentina论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Canc & Blood Disorde, Dana Farber, Padua, Italy Univ Padua, Dept Pediat Hematol & Oncol Ctr, Womans & Child Hlth, Padua, Italy
- [8] Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline ModelMOLECULAR THERAPY, 2017, 25 (04) : 892 - 903Gray-Edwards, Heather L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USARegier, Debra S.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAShirley, Jamie L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Univ Florida, Dept Pediat, Gainesville, FL 32611 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USARandle, Ashley N.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USASalibi, Nouha论文数: 0 引用数: 0 h-index: 0机构: MR R&D Siemens Healthcare, Malvern, PA 19355 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAThomas, Sarah E.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USALatour, Yvonne L.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAJohnston, Jean论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAGolas, Gretchen论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAMaguire, Annie S.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USATaylor, Amanda R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Dept Clin Sci, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USASorjonen, Donald C.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Dept Clin Sci, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAMcCurdy, Victoria J.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Mississippi State Univ, Dept Biol Sci, Mississippi State, MS 39762 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAChristopherson, Peter W.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Dept Pathobiol, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USABradbury, Allison M.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Univ Penn, Sch Vet Med, Dept Clin Sci, Philadelphia, PA 19104 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USABeyers, Ronald J.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Dept Elect & Comp Engn, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAJohnson, Aime K.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Dept Clin Sci, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USABrunson, Brandon L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USACox, Nancy R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Dept Pathobiol, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USABaker, Henry J.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USADenney, Thomas S.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Dept Elect & Comp Engn, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Med Sch, Dept Neurol, Worcester, MA 01655 USA Univ Massachusetts, Med Sch, Gene Therapy Ctr, Worcester, MA 01655 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USATifft, Cynthia J.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Coll Vet Med, Scott Ritchey Res Ctr, 1265 HC Morgan Dr, Auburn, AL 36849 USA
- [9] Cerebrospinal Fluid for Delivery of AAV Gene Therapy in GM1 GangliosidosisMOLECULAR THERAPY, 2016, 24 : S240 - S240Gross, Amanda L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAGray-Edwards, Heather论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMurdock, Bryan论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA论文数: 引用数: h-index:机构:Brunson, Brandon论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USARandle, Ashley N.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAStocia, Lorelei论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USATodessa, Sophia论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USALata, Jaclyn论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Neurol, Worcester, MA USA Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA Auburn Univ, Dept Anat Physiol & Pharmacol, Auburn, AL 36849 USA Auburn Univ, Scott Ritchey Res Ctr, Auburn, AL 36849 USA
- [10] A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosisEBIOMEDICINE, 2023, 92Kell, Pamela论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USASidhu, Rohini论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Casma Therapeut, Cambridge, MA 02139 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAQian, Mingxing论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Dev Biol, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAMishra, Sonali论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USANicoli, Elena-Raluca论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Med Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Off Clin Director, NIH, Bethesda, MD 20892 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAD'Souza, Precilla论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Med Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Off Clin Director, NIH, Bethesda, MD 20892 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USATifft, Cynthia J.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Med Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Off Clin Director, NIH, Bethesda, MD 20892 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAGross, Amanda L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Coll Vet Med, Auburn, AL 36849 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAGray-Edwards, Heather L.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Coll Vet Med, Auburn, AL 36849 USA Univ Massachusetts, Horae Gene Therapy Ctr, Dept Radiol, Med Sch, Worcester, MA 01605 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAMartin, Douglas R.论文数: 0 引用数: 0 h-index: 0机构: Auburn Univ, Scott Ritchey Res Ctr, Coll Vet Med, Auburn, AL 36849 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Dept Neurol, Med Sch, Worcester, MA 01605 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USADietzen, Dennis J.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Pathol & Immunol, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USASingh, Manmilan论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Chem, St Louis, MO 63130 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USALuo, Jingqin论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Surg, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USASchaffer, Jean E.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Harvard Med Sch, Joslin Diabet Ctr, Boston, MA 02215 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAOry, Daniel S.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Casma Therapeut, Cambridge, MA 02139 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USAJiang, Xuntian论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA Washington Univ, Dept Med, Sch Med, St Louis, MO 63110 USA