共 28 条
- [1] Discovering Rationally-Engineered AAV5-derived Capsid Variants for Superior CNS Tropism and Peripheral Tissue De-targeting in Non-Human Primate via Systemic AdministrationMOLECULAR THERAPY, 2024, 32 (05) : 11 - 11Zhu, Sha论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USAWang, Hongxing论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USACabrera, Gabriela Toro论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USAZhang, Weiqun论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USALiu, Na论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USAZhao, Lingzhi论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USAShen, Joan论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut US Inc, Lexington, MA USA NeuShen Therapeut US Inc, Lexington, MA USA
- [2] Directed Evolution of Enhanced AAV Capsid Variants Following Intravitreal Injection in MacaqueINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2017, 58 (08)Boye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAChoudhury, Shreyasi论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMarsic, Damien论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAStrang, Christianne E.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Psychol, Birmingham, AL USA Univ Florida, Ophthalmol, Gainesville, FL USAAlexander, John J.论文数: 0 引用数: 0 h-index: 0机构: Emory Univ, Human Genet, Atlanta, GA 30322 USA Univ Florida, Ophthalmol, Gainesville, FL USAWitherspoon, C. Douglas论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Ophthalmol, Birmingham, AL USA Univ Florida, Ophthalmol, Gainesville, FL USAZolotukhin, Sergei论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAGamlin, Paul D.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Ophthalmol, Birmingham, AL USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Shannon Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USA
- [3] In Vivo Selection of CNS-Specific Novel AAV Capsid Variants by Directed EvolutionMOLECULAR THERAPY, 2018, 26 (05) : 184 - 184Wang, Hongxing论文数: 0 引用数: 0 h-index: 0Ng, Robert论文数: 0 引用数: 0 h-index: 0Joo, Kyeil论文数: 0 引用数: 0 h-index: 0Chen, Qingmin论文数: 0 引用数: 0 h-index: 0Huang, Carol论文数: 0 引用数: 0 h-index: 0Carroll, Jenna论文数: 0 引用数: 0 h-index: 0Goulet, Martin论文数: 0 引用数: 0 h-index: 0Sah, Dinah论文数: 0 引用数: 0 h-index: 0Hou, Jay论文数: 0 引用数: 0 h-index: 0
- [4] AAV9 Capsid Variants with Improved CNS Transduction Identified by Directed EvolutionMOLECULAR THERAPY, 2023, 31 (04) : 661 - 661Rohovie, Marcus论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAKruse, Nikki论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USASchmitt, Christopher论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAWong, Victoria论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USASero, Antoinette论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USARivera-Velazquez, Mirella论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USALee, Grace论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USADesautel, Sarah论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USADel Greco, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USASedighi, Faezeh论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USANivina, Aleksandra论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAJenne, Stephan论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAGebretsadik, Kahsay论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAKumar, Ambuj论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAChng, Chinping论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USAAkeefe, Hassibullah论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USASilverman, Adam论文数: 0 引用数: 0 h-index: 0机构: Codexis Inc, San Carlos, CA USA Codexis Inc, San Carlos, CA USA
- [5] Directed Evolution of AAV9 Libraries in Non-Human Primates Identifies a Capsid Family with Enhanced Central Nervous System Tropism and Liver De-Targeting Following Systemic DeliveryMOLECULAR THERAPY, 2024, 32 (04) : 66 - 66Shi, Xiaojing论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAGross, Sean论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USALing, Michelle论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAElteriefi, Reem论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAMason, Zach论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAHolloway, Caden论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAWang, Yixi论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAChin, Mark论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAMcDowell, Kimberly论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAWheeler, Brandon论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAFlytzanis, Nicholas论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USAGoeden, Nick论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USACatalano, Susan论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut Inc, Thousand Oaks, CA USA Capsida Biotherapeut Inc, Thousand Oaks, CA USA
- [6] Identification of Novel AAV Capsid Variants with Enhanced Tropism for the Canine Outer Retina Following Intravitreal DeliveryMOLECULAR THERAPY, 2016, 24 : S244 - S245Byrne, Leah C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USAVisel, Meike论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USADufour, Valerie论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USAMarinho, Felipe Pompeo论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USAAguirre, Gustavo D.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USABeltran, William A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USAFlannery, John G.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USASchaffer, David V.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Sch Vet Med, Dept Clin Studies, Helen Wills Neurosci Inst,Univ Penn, Berkeley, CA 94720 USA
- [7] Systemic Administration of Novel Engineered AAV Capsids Facilitates Enhanced Transgene Expression in the Macaque Central Nervous SystemMOLECULAR THERAPY, 2022, 30 (04) : 207 - 208Stanton, Alexandra C.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Harvard Univ, Cambridge, MA 02138 USA Harvard Med Sch, Boston, MA 02115 USA Broad Inst, Cambridge, MA USALagerborg, Kim A.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Harvard Univ, Cambridge, MA 02138 USA Harvard Med Sch, Boston, MA 02115 USA Broad Inst, Cambridge, MA USAKrunnfusz, Allison论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Broad Inst, Cambridge, MA USATellez, Liana论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Broad Inst, Cambridge, MA USAKing, Emily M.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Broad Inst, Cambridge, MA USA论文数: 引用数: h-index:机构:Tabebordbar, Mohammadsharif论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Broad Inst, Cambridge, MA USASabeti, Pardis C.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst, Cambridge, MA USA Harvard Univ, Cambridge, MA 02138 USA Broad Inst, Cambridge, MA USA
- [8] A Rationally Engineered Novel Capsid Variant of AAV9 for Pripheral Tissue-Detargeted and CNS-Directed Systemic Gene DeliveryMOLECULAR THERAPY, 2013, 21 : S2 - S2Zhong, Li论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Shaoyong论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Microbio & Physiol Syst, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAVliet, Kim Van论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Mengxin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAXie, Jun论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Jia论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAZhang, Yu论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Huapeng论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAWang, Dan论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGoetzmann, Jason论文数: 0 引用数: 0 h-index: 0机构: Univ Louisiana Lafayette, New Iberia Res Ctr, New Iberia, LA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAFlotte, Terence R.论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Microbio & Physiol Syst, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA
- [9] A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in NeonatesMOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2018, 9 : 234 - 246Wang, Dan论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USALi, Shaoyong论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGessler, Dominic J.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAXie, Jun论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAZhong, Li论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USALi, Jia论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USATran, Karen论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAVan Vliet, Kim论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USARen, Lingzhi论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGoetzmann, Jason E.论文数: 0 引用数: 0 h-index: 0机构: Univ Louisiana Lafayette, New Iberia Res Ctr, New Iberia, LA 70560 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAFlotte, Terence R.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Dept Pediat, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Sichuan Univ, West China Hosp, Chengdu 610041, Sichuan, Peoples R China Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA
- [10] A Rationally Engineered Novel Capsid Variant of AAV9 for Peripheral Tissue-Detargeted and CNS-Directed Systemic Gene DeliveryMOLECULAR THERAPY, 2014, 22 : S112 - S112Zhong, Li论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Shaoyong论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAVan Vliet, Kim论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Mengxin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAXie, Jun论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Jia论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAZhang, Yu论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Huapeng论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAWang, Dan论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGoetzmann, Jason论文数: 0 引用数: 0 h-index: 0机构: Univ Louisiana Lafayette, New Iberia Res Ctr, New Iberia, LA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAFlotte, Terence R.论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA Umass Med Sch, Dept Microbio & Physiol Syst, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA