共 50 条
- [1] Response to Letter to the Editor: Effect of Nusinersen on Respiratory and Bulbar Function in Children with Spinal Muscular AtrophyNEUROPEDIATRICS, 2025, 56 (01) : 63 - 64论文数: 引用数: h-index:机构:Lopez-Lobato, Mercedes论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Neurol Unit, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainValverde-Fernandez, Justo论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Gastroenterol Hepatol & Nutr Unit, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainFerrand-Ferri, Patricia论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen del Rocio, Dept Paediat Phys Med & Rehabil, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainRubio-Perez, Eloisa论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen del Rocio, Fdn Gest Invest Salud Sevilla FISEVI, Methodol & Stat Management Unit, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainAndrade-Ruiz, Henry A.论文数: 0 引用数: 0 h-index: 0机构: Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainGonzalez, Jose M. Lopez-Puerta论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Virgen del Rocio, Dept Orthopaed Surg & Traumatol, Div Spine Surg, Seville, Spain Networking Biomed Res Ctr Bioengn Biomat & Nanomed, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, SpainMadruga-Garrido, Marcos论文数: 0 引用数: 0 h-index: 0机构: Hosp Viamed Santa Angela de la Cruz, Neurol Pediat, Seville, Spain Neurolinkia, Seville, Spain Univ Seville, Hosp Univ Virgen del Rocio, Dept Paediat, Paediat Pulmonol Unit,IBiS ,Inst Biomed Sevilla,CS, Seville, Spain
- [2] Effect of nusinersen on motor, respiratory and bulbar function in early-onset spinal muscular atrophyBRAIN, 2023, 146 (02) : 668 - 677Pechmann, Astrid论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyBehrens, Max论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Med Biometry & Stat, Fac Med, D-70196 Freiburg, Germany Univ Freiburg, Med Ctr, D-70196 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyDoernbrack, Katharina论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Clin Trials Unit, D-79106 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyTassoni, Adrian论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Clin Trials Unit, D-79106 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyStein, Sabine论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyVogt, Sibylle论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyZoeller, Daniela论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Med Biometry & Stat, Fac Med, D-70196 Freiburg, Germany Univ Freiburg, Med Ctr, D-70196 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyBernert, Gunther论文数: 0 引用数: 0 h-index: 0机构: Clin Favoriten, Dept Pediat, A-1100 Vienna, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyHagenacker, Tim论文数: 0 引用数: 0 h-index: 0机构: Univ Med Essen, Dept Neurol, Hufelandstr 55, D-45147 Essen, Germany Univ Med Essen, Ctr Translat Neuro & Behav Sci C TNBS, Hufelandstr 55, D-45147 Essen, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany论文数: 引用数: h-index:机构:Schwersenz, Inge论文数: 0 引用数: 0 h-index: 0机构: Deutsch Gesell Muskelkranke, D-79112 Freiburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyWalter, Maggie C.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, D-80336 Munich, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyBaumann, Matthias论文数: 0 引用数: 0 h-index: 0机构: Med Univ Innsbruck, Dept Pediat 1, Div Pediat Neurol, A-6020 Innsbruck, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyBaumgartner, Manuela论文数: 0 引用数: 0 h-index: 0机构: Ordensklinikum Linz, Dept Pediat & Adolescent Med, A-4020 Linz, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyDeschauer, Marcus论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Sch Med, Dept Neurol, D-81675 Munich, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyEisenkoelbl, Astrid论文数: 0 引用数: 0 h-index: 0机构: Johannes Kepler Univ Linz, Kepler Univ Hosp, Dept Paediat & Adolescent Med, A-4020 Linz, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyFlotats-Bastardas, Marina论文数: 0 引用数: 0 h-index: 0机构: Saarland Univ Hosp, Dept Pediat Neurol, D-66421 Homburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyHahn, Andreas论文数: 0 引用数: 0 h-index: 0机构: Justus Liebig Univ, Dept Child Neurol, D-35392 Giessen, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyHorber, Veronka论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Paediat Neurol, D-72076 Tubingen, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyHusain, Ralf A.论文数: 0 引用数: 0 h-index: 0机构: Jena Univ Hosp, Dept Neuropediat, D-07747 Jena, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyIllsinger, Sabine论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Clin Pediat Kidney Liver & Metab Dis, D-30625 Hannover, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyJohannsen, Jessika论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, D-20246 Hamburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyKoehler, Cornelia论文数: 0 引用数: 0 h-index: 0机构: Ruhr Univ Bochum, Univ Klin Kinder & Jugendmed, Abt Neuropadiatrie & Sozialpadiatrie, St Josef Hosp, D-44791 Bochum, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyKoelbel, Heike论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Ctr Translat Neuro & Behav Sci, Dept Neuropediat, D-45147 Essen, Germany Univ Duisburg Essen, Ctr Translat Neuro & Behav Sci, Neuromuscular Ctr Children & Adolescents, D-45147 Essen, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyMueller, Monika论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Wurzburg, Dept Neuropediat, D-97080 Wurzburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germanyvon Moers, Arpad论文数: 0 引用数: 0 h-index: 0机构: DRK Kliniken Berlin, Dept Pediat & Neuropediat, D-14050 Berlin, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanySchlachter, Kurt论文数: 0 引用数: 0 h-index: 0机构: State Hosp Bregenz LKH Bregenz, Dept Pediat, A-6900 Bregenz, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanySchreiber, Gudrun论文数: 0 引用数: 0 h-index: 0机构: Klinikum Kassel, Dept Pediat Neurol, D-34125 Kassel, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanySchwartz, Oliver论文数: 0 引用数: 0 h-index: 0机构: Munster Univ Hosp, Dept Pediat Neurol, D-48149 Munster, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanySmitka, Martin论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Dresden, Med Fak Carl Gustav Carus, Abt Neuropaediat, D-01307 Dresden, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanySteiner, Elisabeth论文数: 0 引用数: 0 h-index: 0机构: Klinikum Wels Grieskirchen, Dept Pediat, A-4600 Wels, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyStoegmann, Eva论文数: 0 引用数: 0 h-index: 0机构: LK Banden Modling, Dept Pediat, A-2340 Modling, Austria Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyTrollmann, Regina论文数: 0 引用数: 0 h-index: 0机构: Friedrich Alexander Univ Erlangen Nurnberg, Dept Pediat, Div Pediat Neurol, D-91054 Erlangen, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyVill, Katharina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pediat Neurol & Dev Med, Dr von Hauner Childrens Hosp, LMU Hosp, D-80337 Munich, Germany Ludwig Maximilians Univ Munchen, LMU Hosp, Dr von Hauner Childrens Hosp, LMU Ctr Children Med Complex, D-80337 Munich, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyWeiss, Claudia论文数: 0 引用数: 0 h-index: 0机构: Charite Univ Med Berlin, Dept Pediat Neurol, Augustenburger Pl 1, D-13353 Berlin, Germany Charite Univ Med Berlin, Ctr Chronically Sick Children, Augustenburger Pl 1, D-13353 Berlin, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyWiegand, Gert论文数: 0 引用数: 0 h-index: 0机构: Asklepios Clin Hamburg Nord Heidberg, Neuropediat Sect, Dept Pediat, D-22417 Hamburg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyZiegler, Andreas论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Heidelberg, Dept Neuropediat & Metab Med, D-69120 Heidelberg, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyLochmueller, Hanns论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany Childrens Hosp Eastern Ontario Res Inst, Ottawa, ON K1H 8L1, Canada Ottawa Hosp, Dept Med, Div Neurol, Ottawa, ON K1H 8L6, Canada Univ Ottawa, Brain & Mind Res Inst, Ottawa, ON K1H 8M5, Canada Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, GermanyKirschner, Janbernd论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany Univ Hosp Bonn, Dept Neuropediat, Fac Med, D-53127 Bonn, Germany Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, D-79106 Freiburg, Germany
- [3] Effect of Nusinersen on Respiratory and Bulbar Function in Children with Spinal Muscular Atrophy: Real-World Experience from a Single CenterNEUROPEDIATRICS, 2025, 56 (01) : 2 - 11Gaboli, Mirella论文数: 0 引用数: 0 h-index: 0机构: Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainLobato, Mercedes Lopez论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen Rocio, Dept Paediat, Paediat Neurol Unit, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainFernandez, Justo Valverde论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen Rocio, Dept Paediat, Paediat Gastroenterol Hepatol & Nutr Unit, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainFerri, Patricia Ferrand论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen Rocio, Paediat Phys Med & Rehabil Dept, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainPerez, Eloisa Rubio论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen Rocio, Fdn Gest Invest Salud Sevilla FISEVI, Methodol & Stat Management Unit, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainRuiz, Henry A. Andrade论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Virgen Rocio, Fdn Gest Invest Salud Sevilla FISEVI, Methodol & Stat Management Unit, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainGonzalez, Jose Maria Lopez-Puerta论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Virgen Rocio, Networking Biomed Res Ctr Bioengn Biomat & Nanomed, Dept Orthopaed Surg & Traumatol, Spine Surg, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, SpainMadruga-Garrido, Marcos论文数: 0 引用数: 0 h-index: 0机构: Hosp Viamed Santa Angela Cruz, Neurol Pediat, Seville, Spain Neurolinkia, Seville, Spain Univ Seville, Hosp Univ Virgen Rocio, CSIC, Paediat Pulmonol Unit,Dept Paediat,Inst Biomed Se, Seville, Spain
- [4] Evolution of bulbar function in spinal muscular atrophy type 1 treated with nusinersenDEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY, 2022, 64 (07): : 907 - 914Weststrate, Harriet论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandStimpson, Georgia论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandThomas, Lily论文数: 0 引用数: 0 h-index: 0机构: UCL, Dept Language & Commun, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandScoto, Mariacristina论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandJohnson, Emily论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandStewart, Alexandra论文数: 0 引用数: 0 h-index: 0机构: UCL, Dept Language & Commun, London, England Great Ormond St Hosp NHS Fdn Trust, Dept Speech & Language Therapy, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandMuntoni, Francesco论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandBaranello, Giovanni论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, EnglandConway, Eleanor论文数: 0 引用数: 0 h-index: 0机构: NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England Great Ormond St Hosp NHS Fdn Trust, UCL Great Ormond St Inst Child IIealth, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, UCL Great Ormond St Inst Child Hlth, Dev Neurosci Res & Teaching Dept,Dubowitz Neuromu, London, England
- [5] Nusinersen stabilises respiratory function in paediatric spinal muscular atrophyEUROPEAN RESPIRATORY JOURNAL, 2020, 56Chacko, Archana论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Brisbane, Qld, Australia Univ Queensland, Brisbane, Qld, AustraliaDeegan, Sean论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Brisbane, Qld, Australia Univ Queensland, Brisbane, Qld, AustraliaGauld, Leanne论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Brisbane, Qld, Australia Univ Queensland, Brisbane, Qld, Australia论文数: 引用数: h-index:机构:
- [6] The effects of nusinersen treatment on respiratory status of children with spinal muscular atrophyPEDIATRICS INTERNATIONAL, 2022, 64 (01)Hepkaya, Evrim论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeySakalli, Ayse Ayzit Kilinc论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyUlkersoy, Ipek论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat, Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyBaskan, Azer Kilic论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyArslan, Huseyin论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyMeral, Ozge论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyDilek, Tugce Damla论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Neurol, Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyGuler, Serhat论文数: 0 引用数: 0 h-index: 0机构: Biruni Univ, Dept Pediat Neurol, Fac Med, Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeySaltik, Sema论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Neurol, Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, TurkeyCokugras, Haluk论文数: 0 引用数: 0 h-index: 0机构: Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey Istanbul Univ Cerrahpasa, Cerrahpasa Fac Med, Dept Pediat Pulmonol, Cerrahpa Mah Kocamustafapasa Cad 34, TR-34098 Istanbul, Turkey
- [7] Nusinersen improved respiratory function in spinal muscular atrophy type 2PEDIATRICS INTERNATIONAL, 2021, 63 (08) : 973 - 974论文数: 引用数: h-index:机构:Fukushima, Fujiko论文数: 0 引用数: 0 h-index: 0机构: Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, Japan Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, JapanMotoyama, Keiichi论文数: 0 引用数: 0 h-index: 0机构: Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, Japan Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, JapanKobayashi, Chie论文数: 0 引用数: 0 h-index: 0机构: Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, Japan Univ Tsukuba, Ibaraki Pediat Educ & Training Stn, Mito, Ibaraki, Japan Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, JapanIzumi, Isho论文数: 0 引用数: 0 h-index: 0机构: Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, Japan Ibaraki Childrens Hosp, Dept Pediat, Mito, Ibaraki, Japan
- [8] Paediatric spinal muscular atrophy: Longterm nusinersen treatment and respiratory functionRESPIROLOGY, 2022, 27 : 183 - 184Chacko, A.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, AustraliaSly, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Child Hlth Res Ctr, Brisbane, Qld, Australia Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, AustraliaDeegan, S.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, AustraliaThomas, N.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Physiotherapy Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, AustraliaGauld, L.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Resp & Sleep Dept, Brisbane, Qld, Australia
- [9] STABILISATION OF RESPIRATORY FUNCTION IN PAEDIATRIC SPINAL MUSCULAR ATROPHY TREATED WITH NUSINERSENRESPIROLOGY, 2020, 25 : 66 - 66Chacko, A.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, South Brisbane, Qld, Australia Queensland Childrens Hosp, South Brisbane, Qld, AustraliaSly, P.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, South Brisbane, Qld, Australia Queensland Childrens Hosp, South Brisbane, Qld, AustraliaDeegan, S.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, South Brisbane, Qld, Australia Queensland Childrens Hosp, South Brisbane, Qld, AustraliaGauld, L.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, South Brisbane, Qld, Australia Queensland Childrens Hosp, South Brisbane, Qld, Australia
- [10] Stabilization of Respiratory Function in Pediatric Spinal Muscular Atrophy Treated with NusinersenAMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2020, 201Chacko, A.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, AustraliaDeegan, S.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, AustraliaSly, P. D.论文数: 0 引用数: 0 h-index: 0机构: Chlidrens Hlth Queensland, Ctr Childrens Hlth Res, South Brisbane, Australia Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, AustraliaGauld, L.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, Australia Queensland Childrens Hosp, Queensland Childrens Resp & Sleep Dept, Brisbane, Qld, Australia