An Optimized System for AAV Compatible Delivery of Full Length PCDH15 for Treatment of USH1F via RNA End Joining

被引：0
|
作者：
Williams, Claire E. [1 ]
Hsu, Ryan H. [2 ,3 ]
Hermann, Kip J. [1 ]
Bachmann, Lukas C. [4 ]
Pfaff, Samuel L. [1 ]
机构：
[1] Salk Inst Biol Studies, San Diego, CA USA
[2] Salk Inst Biol Studies, La Jolla, CA USA
[3] Univ Calif San Diego, La Jolla, CA USA
[4] Insmed Inc, San Diego, CA USA
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1628
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收藏
页码：760 / 760
页数：1
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