Preclinical development of SENS-501 as a treatment for the autosomal recessive non-syndromic deafness 9 (DFNB9) using an adeno associated vector-based gene therapy

被引：0

作者：

Rambeau, P. ^{[1
]}

Olivier, G. ^{[1
]}

Van Ba, C. Tran ^{[1
]}

Barrot, L. ^{[1
]}

Boudra, R. ^{[1
]}

Dos Reis, J. Duron ^{[1
]}

Vaux, C. ^{[1
]}

Pierredon, S. ^{[1
]}

Pages, A. ^{[1
]}

Liaudet, P. ^{[1
]}

Broussy, A. ^{[1
]}

Harrus, A. G. ^{[1
]}

Dadak, S. ^{[1
]}

Gallot, L. ^{[1
]}

Petit, G. ^{[1
]}

Nevoux, J.

Lahlou, G.

Loundon, N.

Le Bec, C.

Bousquet, E. ^{[1
]}

Lecomte, M. J. ^{[2
,3
]}

Safieddine, S. ^{[2
,3
]}

Petit, C. ^{[3
]}

Giese, A. ^{[1
]}

Desire, L. ^{[1
]}

机构：

[1] Sensorion, Montpellier, France

[2] Genet & Physiol Hearing Lab, Paris, France

[3] Inst Pasteur, Inst Audit, Paris, France

来源：

HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P011

引用

页码：A49 / A49

页数：1

共 9 条

[1] Preclinical Development of an Adeno Associated Vector-Based Gene Therapy (SENS-501) for the Autosomal Recessive Non-Syndromic Deafness 9 (DFNB9)
Olivier, Guillaume
Van Ba, Christophe Tran
Barrot, Lise
Boudra, Rafik
Dos Reis, Julie Duron
Rambeau, Pierre
Vaux, Charlene
Pierredon, Sandra
Riviere, Anais
Liaudet, Pauline
Broussy, Audrey
Harrus, Anne-Gabrielle
Dadak, Selma
Safieddine, Saaid
Nevoux, Jerome
Lahlou, Ghizlene
Loundon, Natalie
Le Bec, Christine
Bousquet, Emilie
Lecomte, Marie-Jose
Petit, Christine
Giese, Arnaud
Desire, Laurent
MOLECULAR THERAPY, 2023, 31 (04) : 459 - 460
[2] Preclinical Development of SENS-501 as a Treatment for the Autosomal Recessive Non-Syndromic Deafness 9 (DFNB9) Using an Adeno Associated Vector-Based Gene Therapy
Boudra, Rafik
Olivier, Guillaume
Van Ba, Christophe Tran
Barrot, Lise
Dos Reis, Julie Duron
Rambeau, Pierre
Vaux, Charlene
Pierredon, Sandra
Pages, Anais
Liaudet, Pauline
Broussy, Audrey
Harrus, Anne-Gabrielle
Dadak, Selma
Gallot, Laura
Petit, Geraldine
Nevoux, Jerome
Lahlou, Ghizlene
Loundon, Natalie
Le Bec, Christine
Bousquet, Emilie
Lecomte, Marie-Jose
Safieddine, Said
Petit, Christine
Giese, Arnaud
Desire, Laurent
MOLECULAR THERAPY, 2024, 32 (04) : 696 - 697
[3] Adeno Associated Vector-Based Gene Therapy for the Autosomal Recessive Non-Syndromic Deafness 9 (DFNB9)
Olivier, G.
Van Ba, C. Tran
Giese, A. P. J.
Vidal, P.
Barrot, L.
Rambeau, P.
Broussy, A.
Nevoux, J.
Lahlou, G.
Loundon, N.
Fiteni, E.
Vaux, C.
Le Bec, C.
Bousquet, E.
Vasseur, A.
Lecomte, M. J.
Safieddine, S.
Petit, C.
Yang, N.
Desire, L.
HUMAN GENE THERAPY, 2022, 33 (23-24) : A80 - A80
[4] Novel Adeno Associated Vector-Based Gene Therapy for the Autosomal Recessive Non-syndromic Deafness (DFNB9)
Nevoux, Jerome
Lalhou, Ghizlene
Plion, Baptiste
Alciato, Lauranne
Giorgi, Marie
Calvet, Charlotte
Ciric, Danica
Vidal, Patrice
Desire, Laurent
Lecomte, Marie-Jose
Petit, Christine
Safieddine, Saaid
MOLECULAR THERAPY, 2021, 29 (04) : 176 - 176
[5] A second Middle Eastern kindred with autosomal recessive non-syndromic hearing loss segregates DFNB9
Suzanne M Leal
Fazil Apaydin
Carol Barnwell
Metin Iber
Tolga Kandogan
Markus Pfister
Uwe Braendle
Orhan Cura
Marvin Schwalb
Hans-Peter Zenner
Emilia Vitale
European Journal of Human Genetics, 1998, 6 : 341 - 344
[6] A second Middle Eastern kindred with autosomal recessive non-syndromic hearing loss segregates DFNB9
Leal, SM
Apaydin, F
Barnwell, C
Iber, M
Kandogan, T
Pfister, M
Braendle, U
Cura, O
Schwalb, M
Zenner, HP
Vitale, E
EUROPEAN JOURNAL OF HUMAN GENETICS, 1998, 6 (04) : 341 - 344
[7] Screening for DFNB1, DFNB2, DFNB3, DFNB4, DFNB9 and DFNB21 loci in the Iranian patients with autosomal recessive non-syndromic hearing loss
Riazalhosseini, Y
Daneshi, A
Imanirad, P
Mohseni, M
Bazazzadegan, N
Kahrizi, K
Farhadi, M
Dalgleish, R
Najmabadi, H
JOURNAL OF MEDICAL GENETICS, 2005, 42 : S102 - S102
[8] Genetic Linkage Analysis of DFNB3, DFNB9 and DFNB21 Loci in GJB2 Negative Families with Autosomal Recessive Non-syndromic Hearing Loss
Masoudi, Marjan
Ahangari, Najmeh
Poursadegh Zonouzi, Ali Akbar
Poursadegh Zonouzi, Ahmad
Nejatizadeh, Azim
IRANIAN JOURNAL OF PUBLIC HEALTH, 2016, 45 (05) : 680 - 687
[9] Further Refinement of the Gene Therapy Treatment and Vector for AB-Variant GM2 Gangliosidoses in a Mouse Model Using Self-Complimentary Adeno-Associated Virus Serotype 9
Deschenes, Natalie M.
Kot, Shalini
Chen, Zhilin
Rykman, Alex E.
Quinville, Brianna M.
Jadav, Anish
Mitchell, Melissa
Gray, Steven
Walia, Jagdeep S.
MOLECULAR THERAPY, 2019, 27 (04) : 262 - 263

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