Interim results from a phase 2, open-label study evaluating an oral, fixed-dose combination of sodium phenylbutyrate and taurursodiol in wolfram syndrome (HELIOS)

被引：0
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作者：
Urano, F. [1 ]
Hurst, S. [1 ]
Marshall, B. [2 ]
Erpelding, N. [3 ]
Cottrell, K. [3 ]
Leinders, M. [3 ]
Mehta, L. [3 ]
机构：
[1] Washington Univ, Sch Med, Dept Med, Div Endocrinol Metab & Lipid Res, St Louis, MO 63110 USA
[2] Washington Univ, Sch Med, Dept Pediat, Div Endocrinol & Diabet, St Louis, MO 63110 USA
[3] Amylyx Pharmaceut, Cambridge, MA USA
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2024年 / 97卷
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
O-34
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页码：50 / 50
页数：1
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