共 50 条
- [1] Chemical Design of Oligonucleotides That Support Targeted RNA Editing in the CNS of Non-Human PrimatesMOLECULAR THERAPY, 2024, 32 (04) : 560 - 561Shivalila, Chikdu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USALu, Genliang论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAAcker, Christopher论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAHarding, Ian论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USADesai, Jigar论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAGodfrey, Jack论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAIwamoto, Naoki论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAKandasamy, Pachamuthu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAYu, Hui论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAKawamoto, Tomomi论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAMetterville, Jake论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USACannon, Megan论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAErin, Purcell-Estabrook论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAAlyse, Faraone论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAMonian, Prashant论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAStandley, Stephany论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USATurner, Jesse论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAYordanoff, Ryan论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USALiu, Fangjun论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAYang, Hailin论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAByrne, Michael论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USAVargeese, Chandra论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA USA Wave Life Sci, Cambridge, MA USA
- [2] Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotidesNature Biotechnology, 2022, 40 : 1093 - 1102Prashant Monian论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Chikdu Shivalila论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Genliang Lu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Mamoru Shimizu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,David Boulay论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Karley Bussow论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Michael Byrne论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Adam Bezigian论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Arindom Chatterjee论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,David Chew论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Jigar Desai论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Frank Favaloro论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Jack Godfrey论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Andrew Hoss论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Naoki Iwamoto论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Tomomi Kawamoto论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Jayakanthan Kumarasamy论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Anthony Lamattina论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Amber Lindsey论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Fangjun Liu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Richard Looby论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Subramanian Marappan论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Jake Metterville论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Ronelle Murphy论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Jeff Rossi论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Tom Pu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Bijay Bhattarai论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Stephany Standley论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Snehlata Tripathi论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Hailin Yang论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Yuan Yin论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Hui Yu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Cong Zhou论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Luciano H. Apponi论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Pachamuthu Kandasamy论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,Chandra Vargeese论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sciences,
- [3] Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotidesNATURE BIOTECHNOLOGY, 2022, 40 (07) : 1093 - +Monian, Prashant论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAShivalila, Chikdu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USALu, Genliang论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAShimizu, Mamoru论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USABoulay, David论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USABussow, Karley论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAByrne, Michael论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USABezigian, Adam论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAChatterjee, Arindom论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAChew, David论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USADesai, Jigar论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAFavaloro, Frank论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAGodfrey, Jack论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAHoss, Andrew论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAIwamoto, Naoki论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAKawamoto, Tomomi论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAKumarasamy, Jayakanthan论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USALamattina, Anthony论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USALindsey, Amber论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USALiu, Fangjun论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USALooby, Richard论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAMarappan, Subramanian论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAMetterville, Jake论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAMurphy, Ronelle论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USARossi, Jeff论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAPu, Tom论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USABhattarai, Bijay论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAStandley, Stephany论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USATripathi, Snehlata论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAYang, Hailin论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAYin, Yuan论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAYu, Hui论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAZhou, Cong论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAApponi, Luciano H.论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAKandasamy, Pachamuthu论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USAVargeese, Chandra论文数: 0 引用数: 0 h-index: 0机构: Wave Life Sci, Cambridge, MA 02138 USA Wave Life Sci, Cambridge, MA 02138 USA
- [4] Genome editing and disease modeling in non-human primatesCANCER SCIENCE, 2022, 113 : 634 - 634Aida, Tomomi论文数: 0 引用数: 0 h-index: 0机构: MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Stanley Ctr, Cambridge, MA 02142 USA MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
- [5] Base editing takes a shot at disease in non-human primatesNATURE REVIEWS GENETICS, 2021, 22 (08) : 479 - 479Koch, Linda论文数: 0 引用数: 0 h-index: 0机构: Nature Reviews Genetics,
- [6] Base editing takes a shot at disease in non-human primatesNature Reviews Genetics, 2021, 22 : 479 - 479Linda Koch论文数: 0 引用数: 0 h-index: 0机构: Nature Reviews Genetics,
- [7] Efficient and Safe RNA Editing in Non-Human Primates Using AAV Delivered LEAPER AgentsMOLECULAR THERAPY, 2023, 31 (04) : 126 - 127Yuan, Pengfei论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R ChinaYi, Zexuan论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R ChinaZhao, Yanxia论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R ChinaTang, Gangbin论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R ChinaZhang, Yongjian论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R ChinaHu, Jun论文数: 0 引用数: 0 h-index: 0机构: EdiGene Inc, Beijing, Peoples R China EdiGene Inc, Beijing, Peoples R China
- [8] Efficient In Vivo Gene Editing of Inherited Retinal Disease Genes in Mice and Non-Human PrimatesMOLECULAR THERAPY, 2017, 25 (05) : 353 - 354Boye, Shannon论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAStefanidakis, Michael论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAMepani, Rina论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USASkor, Maxwell N.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAGloskowski, Sebastian W.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAHorng, Joy论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAMcCullough, Kevin T.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAMarco, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAGiannoukos, Georgia论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USACiulla, Dawn论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAChao, Hoson论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USABounoutas, George S.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAWitherspoon, C. Douglas论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Dept Ophthalmol, Birmingham, AL 35294 USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAWilson, Christopher论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USABumcrot, David论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAGamlin, Paul论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Dept Ophthalmol, Birmingham, AL 35294 USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USABoye, Sanford论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAJiang, Haiyan论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAAlbright, Charlie论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USAMaeder, Morgan L.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USA
- [9] Base editing the synapse: Modeling a complex neurological disorder in non-human primatesMOLECULAR THERAPY, 2022, 30 (06) : 2114 - 2116Prosser, Benjamin L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Physiol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Penn Muscle Inst, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Physiol, Philadelphia, PA 19104 USAHelbig, Ingo论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Neurol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Epilepsy NeuroGenet Initiat ENGIN, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Dept Biomed & Hlth Informat DBHi, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Physiol, Philadelphia, PA 19104 USA
- [10] RNA Editing Therapy in a Humanized Mouse Model of MECP2 Duplication Syndrome and Non-Human PrimatesMOLECULAR THERAPY, 2023, 31 (04) : 18 - 19Wu, Xiaoqing论文数: 0 引用数: 0 h-index: 0机构: HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China HuidaGene Therapeut Co Ltd, Shanghai, Peoples R ChinaYang, Dong论文数: 0 引用数: 0 h-index: 0机构: HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China Chinese Acad Sci, Ctr Excellence Brain Sci & Intelligence Technol, Shanghai, Peoples R China HuidaGene Therapeut Co Ltd, Shanghai, Peoples R ChinaShi, Linyu论文数: 0 引用数: 0 h-index: 0机构: HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China HuidaGene Therapeut Co Ltd, Shanghai, Peoples R ChinaYang, Hui论文数: 0 引用数: 0 h-index: 0机构: HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China Chinese Acad Sci, Ctr Excellence Brain Sci & Intelligence Technol, Shanghai, Peoples R China HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China