Alpha-synuclein lowering and rescue of motor phenotype by miRNA-based AAV gene therapy in an in vivo Parkinson's disease rat model

被引：0
|
作者：
Broekmans, S. Acar [1 ]
Erbrink, R. van Westen [1 ]
van Rooijen, C. [1 ]
Toonen, L. [1 ]
Valls, M. [1 ]
Valles, A. [1 ]
机构：
[1] UniQure Biopharma BV, Amsterdam, Netherlands
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P420
引用
收藏
页码：A188 / A189
页数：2
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