Creation of an AAV-Based Replication Origin for Novel AAV Vectors That Cannot Be Replicated in Nature

被引:0
|
作者
Whitfield, Leah R. [1 ]
Inbari, Shani [1 ]
Sutton, R. Bryan [2 ]
Samulski, R. Jude [3 ]
Hirsch, Matthew L. [1 ]
机构
[1] Univ N Carolina, Chapel Hill, NC USA
[2] Texas Tech Univ, Dept Cell Physiol & Mol Biophys, Hlth Sci Ctr, Lubbock, TX USA
[3] UNC Gene Therapy Vector Core, Chapel Hill, NC USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
267.
引用
收藏
页码:143 / 144
页数:2
相关论文
共 50 条
  • [1] AAV-microbead conjugates for the enhanced delivery of AAV-based vectors
    Farlow, SJ
    Pandori, MW
    Sano, T
    MOLECULAR THERAPY, 2004, 9 : S164 - S164
  • [2] Development of the novel AAV-based vectors with selective tropism to human cancer cells
    Sayroo, Rana
    Yin, Zifei
    Nolasco, Diego
    Pandya, Munjal
    Ling, Chen
    Aslanidi, George
    CANCER RESEARCH, 2015, 75
  • [3] A novel platform for engineered AAV-based vaccines
    Babutzka, Sabrina
    Gehrke, Miranda
    Papadopoulou, Anastasia
    Diedrichs-Moehring, Maria
    Giannaki, Maria
    Hennis, Lena
    Foehr, Bastian
    Kooyman, Cale
    Osterman, Andreas
    Yannaki, Evangelia
    Wildner, Gerhild
    Ammer, Hermann
    Michalakis, Stylianos
    MOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2025, 33 (01)
  • [4] A novel AAV-based gene therapy for glaucoma
    Wu, Ling
    Maturana, Carola
    Yao, Zuliang
    Wang, Wei
    Liang, Bo
    Hong, Laura
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2024, 65 (07)
  • [5] TYMS as a novel target for AAV-based therapy
    Vijayakurup, Vinod
    Meyer, Benjamin
    Nawab, Akbar
    Kaye, Frederic J.
    Guijarro, Maria V.
    Zajac-Kaye, Maria
    CANCER RESEARCH, 2023, 83 (07)
  • [6] In Vivo Potency Assay for AAV-Based Gene Therapy Vectors
    De, Bishnu P.
    Chen, Alvin
    Rosenberg, Jonathan B.
    Chiuchiolo, Maria
    Van de Graaf, Benjamin
    Pagovich, Odelya E.
    Sondhi, Dolan
    Russo, Carlo
    Kaminsky, Stephen M.
    Crystal, Ronald G.
    MOLECULAR THERAPY, 2016, 24 : S186 - S186
  • [7] Manufacturing and characterizing AAV-based vectors for use in clinical studies
    Wright, J. F.
    GENE THERAPY, 2008, 15 (11) : 840 - 848
  • [8] Manufacturing and characterizing AAV-based vectors for use in clinical studies
    J F Wright
    Gene Therapy, 2008, 15 : 840 - 848
  • [9] A novel platform for engineered AAV-based vaccines
    Babutzka, S.
    Zobel, L.
    Bogedein, J.
    Diedrichs-Moehring, M.
    Gehrke, M.
    Wildner, G.
    Ammer, H.
    Michalakis, S.
    HUMAN GENE THERAPY, 2022, 33 (23-24) : A210 - A210
  • [10] Developing a Potency Assay for AAV-Based Genome Editing Vectors
    Cummings, Chris
    Hayes, Ryan
    Drouin, Lauren M.
    Hebben, Matthias
    MOLECULAR THERAPY, 2020, 28 (04) : 194 - 194