Recent advances in treatments for congenital adrenal hyperplasia

被引：0
|
作者：
Falhammar, Henrik [1 ,2 ]
Lajic, Svetlana [3 ,4 ,5 ]
Nordenstrom, Anna [3 ,4 ]
机构：
[1] Karolinska Inst, Dept Mol Med & Surg, Stockholm, Sweden
[2] Karolinska Univ Hosp, Dept Endocrinol, Stockholm, Sweden
[3] Karolinska Inst, Dept Womens & Childrens Hlth, Stockholm, Sweden
[4] Karolinska Univ Hosp, Pediat Endocrinol Unit, Stockholm, Sweden
[5] Univ Gothenburg, Sahlgrenska Acad, Dept Clin Sci, Gothenburg, Sweden
来源：
NATURE REVIEWS ENDOCRINOLOGY | 2025年 / 21卷 / 04期
关键词：
D O I：
10.1038/s41574-025-01089-w
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
The first CRFR1 antagonist (crinecerfont) to be used for the treatment of congenital adrenal hyperplasia recently received FDA approval. This Clinical Outlook discusses the latest phase III studies in children and adults, as well as how crinecerfont - in combination with glucocorticoid replacement - might change clinical practice and affect long-term co morbidities.
引用
收藏
页码：197 / 198
页数：2
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