Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell-Type-Specific Gene Editing

被引:0
|
作者
机构
[1] [1,Rouet, Romain
[2] Thuma, Benjamin A.
[3] Roy, Marc D.
[4] Lintner, Nathanael G.
[5] Rubitski, David M.
[6] Finley, James E.
[7] Wisniewska, Hanna M.
[8] 2,Mendonsa, Rima
[9] 2,Hirsh, Ariana
[10] 2,De Oñate, Lorena
[11] 2,Compte Barrón, Joan
[12] McLellan, Thomas J.
[13] Bellenger, Justin
[14] Feng, Xidong
[15] Varghese, Alison
[16] Chrunyk, Boris A.
[17] Borzilleri, Kris
[18] Hesp, Kevin D.
[19] 1,Zhou, Kaihong
[20] 1,Ma, Nannan
[21] Tu, Meihua
[22] Dullea, Robert
[23] McClure, Kim F.
[24] 2,Wilson, Ross C.
[25] Liras, Spiros
[26] Mascitti, Vincent
[27] 1,2,3,4,5,Doudna, Jennifer A.
关键词
Number:; 86059; Acronym:; -; Sponsor:; APP1090875; Sponsor: National Health and Medical Research Council;
D O I
暂无
中图分类号
学科分类号
摘要
引用
收藏
相关论文
共 50 条
  • [1] Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell-Type-Specific Gene Editing
    Rouet, Romain
    Thuma, Benjamin A.
    Roy, Marc D.
    Lintner, Nathanael G.
    Rubitski, David M.
    Finley, James E.
    Wisniewska, Hanna M.
    Mendonsa, Rima
    Hirsh, Ariana
    de Onate, Lorena
    Barron, Joan Compte
    McLellan, Thomas J.
    Bellenger, Justin
    Feng, Xidong
    Varghese, Alison
    Chrunyk, Boris A.
    Borzilleri, Kris
    Hesp, Kevin D.
    Zhou, Kaihong
    Ma, Nannan
    Tu, Meihua
    Dullea, Robert
    McClure, Kim F.
    Wilson, Ross C.
    Liras, Spiros
    Mascitti, Vincent
    Doudna, Jennifer A.
    JOURNAL OF THE AMERICAN CHEMICAL SOCIETY, 2018, 140 (21) : 6596 - 6603
  • [2] Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell Type Specific Gene Editing
    Roy, Marc
    Rouet, Romain
    Thuma, Benjamin
    Lintner, Nathanael
    Rubitski, David
    Finley, James
    Wisniewska, Hanna
    Mendonsa, Rima
    de Onate, Lorena
    Hirsh, Ariana
    Barron, Joan Compte
    McLellan, Thomas
    Bellenger, Justin
    Feng, Xidong
    Varghese, Alison
    Chrunyk, Boris
    Borzilleri, Kris
    Hesp, Kevin
    FASEB JOURNAL, 2018, 32 (01):
  • [3] Cell-type-specific genome editing with a microRNA-responsive CRISPR-Cas9 switch
    Hirosawa, Moe
    Fujita, Yoshihiko
    Parr, Callum J. C.
    Hayashi, Karin
    Kashida, Shunnichi
    Hotta, Akitsu
    Woltjen, Knut
    Saito, Hirohide
    NUCLEIC ACIDS RESEARCH, 2017, 45 (13)
  • [4] Delivery of an endosomolytic CRISPR-Cas9 RNP via receptor-mediated endocytosis for cell-targeted genome editing
    de Onate, L.
    Foss, D.
    Mendonsa, R.
    Wilson, R.
    HUMAN GENE THERAPY, 2019, 30 (11) : A198 - A198
  • [5] Identification of a novel ASGPr ligand and application to receptor mediated delivery and celltype specific gene editing with CRISPR-Cas9 ribonucleoproteins
    Thuma, Benjamin
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2019, 258
  • [6] CRISPR-Cas9 gene editing: Delivery aspects and therapeutic potential
    Blenke, Erik Oude
    Evers, Martijn J. W.
    Mastrobattista, Enrico
    van der Oost, John
    JOURNAL OF CONTROLLED RELEASE, 2016, 244 : 139 - 148
  • [7] Controlling CRISPR-Cas9 Gene Editing
    Dowdy, Steven F.
    NEW ENGLAND JOURNAL OF MEDICINE, 2019, 381 (03): : 289 - 290
  • [8] Exosome-mediated delivery of CRISPR-Cas9: A revolutionary approach to cancer gene editing
    Balaraman, Ashok Kumar
    Babu, M. Arockia
    Moglad, Ehssan
    Mandaliya, Viralkumar
    Rekha, M. M.
    Gupta, Sofia
    Prasad, G. V. Siva
    Kumari, Mukesh
    Chauhan, Ashish Singh
    Ali, Haider
    Goyal, Kavita
    PATHOLOGY RESEARCH AND PRACTICE, 2025, 266
  • [9] Introduction to CRISPR-Cas9 Gene Editing
    Mason, J. M.
    BIRTH DEFECTS RESEARCH, 2020, 112 (11): : 809 - 809
  • [10] Delivery of an Endosomolytic CRISPR-Cas9 RNP Enzyme via Receptor-Mediated Endocytosis for Targeted Genome Editing of T Cells
    Wilson, Ross
    de Onate, Lorena
    Foss, Dana
    Mendonsa, Rima
    MOLECULAR THERAPY, 2020, 28 (04) : 472 - 472