Revolutionizing genetic disease treatment: The case of exagamglogene autotemcel

被引:0
|
作者
Rao, Shuquan [1 ]
Yao, Yao [1 ]
Huo, Wenxuan [2 ,3 ]
Cao, Yang [4 ,5 ]
Budde, Lihua E. [6 ]
机构
[1] Chinese Acad Med Sci & Peking Union Med Coll, State Key Lab Expt Hematol, Inst Hematol & Blood Dis Hosp, Tianjin, Peoples R China
[2] Peking Univ Peoples Hosp, Peking Univ Inst Hematol, Natl Clin Res Ctr Hematol Dis, Beijing 100044, Peoples R China
[3] Chinese Acad Med Sci 2019RU029, Key Tech Diag & Treatments Hematol Malignancies, Res Unit, Beijing 100044, Peoples R China
[4] Huazhong Univ Sci & Technol, Dept Hematol, Wuhan 430030, Peoples R China
[5] Huazhong Univ Sci & Technol, Tongji Hosp, Tongji Med Coll, Canc Biol Res Ctr, Wuhan 430030, Peoples R China
[6] City Hope Natl Med Ctr, Dept Hematol & Hematopoiet Stem Cell Transplantat, Duarte, CA 91010 USA
来源
INNOVATION | 2024年 / 5卷 / 03期
关键词
D O I
10.1016/j.xinn.2024.100619
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页数:2
相关论文
共 50 条
  • [1] Exagamglogene Autotemcel for Severe Sickle Cell Disease
    Frangoul, Haydar
    Locatelli, Franco
    Sharma, Akshay
    Bhatia, Monica
    Mapara, Markus
    Molinari, Lyndsay
    Wall, Donna
    Liem, Robert I.
    Telfer, Paul
    Shah, Ami J.
    Cavazzana, Marina
    Corbacioglu, Selim
    Rondelli, Damiano
    Meisel, Roland
    Dedeken, Laurence
    Lobitz, Stephan
    de Montalembert, Mariane
    Steinberg, Martin H.
    Walters, Mark C.
    Bower, Laura
    Imren, Suzan
    Simard, Christopher
    Xuan, Fengjuan
    Zhou, Weiyu
    Morrow, Phuong Khanh
    Hobbs, William
    Grupp, Stephan
    BLOOD, 2023, 142
  • [2] Exagamglogene Autotemcel for Severe Sickle Cell Disease
    Frangoul, H.
    Locatelli, F.
    Sharma, A.
    Bhatia, M.
    Mapara, M.
    Molinari, L.
    Wall, D.
    Liem, R. I.
    Telfer, P.
    Shah, A. J.
    Cavazzana, M.
    Corbacioglu, S.
    Rondelli, D.
    Meisel, R.
    Dedeken, L.
    Lobitz, S.
    de Montalembert, M.
    Steinberg, M. H.
    Walters, M. C.
    Eckrich, M. J.
    Imren, S.
    Bower, L.
    Simard, C.
    Zhou, W.
    Xuan, F.
    Morrow, P. K.
    Hobbs, W. E.
    Grupp, S. A.
    NEW ENGLAND JOURNAL OF MEDICINE, 2024, 390 (18): : 1649 - 1662
  • [3] Good Results for Exagamglogene autotemcel
    Krome, Susanne
    TRANSFUSIONSMEDIZIN, 2024, 14 (03) : 131 - 131
  • [4] Exagamglogene Autotemcel: First Approval
    Hoy, Sheridan M.
    MOLECULAR DIAGNOSIS & THERAPY, 2024, 28 (02) : 133 - 139
  • [5] Exagamglogene Autotemcel: First Approval
    Sheridan M. Hoy
    Molecular Diagnosis & Therapy, 2024, 28 : 133 - 139
  • [6] Studies of Exagamglogene Autotemcel - Age and Place
    Min, Jie
    NEW ENGLAND JOURNAL OF MEDICINE, 2024, 391 (06): : 571 - 572
  • [7] Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
    Locatelli, F.
    Lang, P.
    Wall, D.
    Meisel, R.
    Corbacioglu, S.
    Li, A. M.
    de la Fuente, J.
    Shah, A. J.
    Carpenter, B.
    Kwiatkowski, J. L.
    Mapara, M.
    Liem, R. I.
    Cappellini, M. D.
    Algeri, M.
    Kattamis, A.
    Sheth, S.
    Grupp, S.
    Handgretinger, R.
    Kohli, P.
    Shi, D.
    Ross, L.
    Bobruff, Y.
    Simard, C.
    Zhang, L.
    Morrow, P. K.
    Hobbs, W. E.
    Frangoul, H.
    NEW ENGLAND JOURNAL OF MEDICINE, 2024, 390 (18): : 1663 - 1676
  • [8] An evaluation of exagamglogene autotemcel for the treatment of sickle cell disease and transfusion-dependent beta-thalassaemia
    Handgretinger, Rupert
    Mezger, Markus
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2024, 24 (09) : 883 - 888
  • [9] Exagamglogene autotemcel: a beacon of hope for severe sickle cell disease and thalassemia management
    Anand, Ayush
    Singh, Mahendra P.
    Sharma, Rakesh K.
    Khatib, Mahalaqua N.
    Gaidhane, Shilpa
    Zahiruddin, Quazi S.
    Rustagi, S.
    Melese, Endalkachew B.
    INTERNATIONAL JOURNAL OF SURGERY OPEN, 2024, 62 (04) : 507 - 508
  • [10] Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Severe Sickle Cell Disease
    Frangoul, Haydar
    Locatelli, Franco
    Bhatia, Monica
    Mapara, Markus Y.
    Molinari, Lyndsay
    Sharma, Akshay
    Lobitz, Stephan
    de Montalembert, Mariane
    Rondelli, Damiano
    Steinberg, Martin
    Walters, Mark C.
    Imren, Suzan
    Zhang, Lanju
    Sharma, Anjali
    Song, Yang
    Simard, Christopher
    Hobbs, William
    Grupp, Stephen
    BLOOD, 2022, 140