ASO-mediated Dnm2 knockdown ameliorates the centronuclear myopathy phenotype of Dnm2RW/+ mice in a dose-dependent manner after disease onset

被引：0
|
作者：
Depla, M. [1 ]
Robe, A. [1 ]
Buono, S. [1 ]
Koch, C. [1 ]
Bitoun, M. [2 ]
Colombo, S. [1 ]
Cowling, B. [1 ]
机构：
[1] Dynacure, Illkirch Graffenstaden, France
[2] Sorbonne Univ, Inst Myol, INSERM, Paris, France
来源：
NEUROMUSCULAR DISORDERS | 2021年 / 31卷
关键词：
D O I：
10.1016/j.nmd.2021.07.053
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
EP.28
引用
收藏
页码：S58 / S58
页数：1
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