[1] Emory Univ, Dept Pediat, Atlanta, GA USA
[2] Childrens Healthcare Atlanta, Atlanta, GA USA
[3] Michigan State Univ, Dept Pediat & Human Dev, E Lansing, MI USA
[4] Birmingham Childrens Hosp, Dept Paediat Haematol, Birmingham, W Midlands, England
[5] Sanofi, Cambridge, MA USA
[6] Sanofi, Gentilly, France
[7] Sanofi, Zug, Switzerland
[8] Sobi, Stockholm, Sweden