ENZYME THERAPY IN GAUCHER DISEASE TYPE-1 - COMPARATIVE EFFICACY OF MANNOSE-TERMINATED GLUCOCEREBROSIDASE FROM NATURAL AND RECOMBINANT SOURCES

被引:0
|
作者
GRABOWSKI, GA
BARTON, NW
PASTORES, G
DAMBROSIA, JM
BANERJEE, TK
MCKEE, MA
PARKER, C
SCHIFFMANN, R
HILL, SC
BRADY, RO
机构
[1] CHILDRENS HOSP MED CTR,CINCINNATI,OH 45229
[2] CUNY MT SINAI SCH MED,DEPT PEDIAT,NEW YORK,NY 10029
[3] CUNY MT SINAI SCH MED,DEPT HUMAN GENET,NEW YORK,NY 10029
[4] NINCDS,DEV & METAB NEUROL BRANCH,BETHESDA,MD 20892
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:A226 / A226
页数:1
相关论文
共 50 条
  • [1] ENZYME THERAPY IN TYPE-1 GAUCHER DISEASE - COMPARATIVE EFFICACY OF MANNOSE-TERMINATED GLUCOCEREBROSIDASE FROM NATURAL AND RECOMBINANT SOURCES
    GRABOWSKI, GA
    BARTON, NW
    PASTORES, G
    DAMBROSIA, JM
    BANERJEE, TK
    MCKEE, MA
    PARKER, C
    SCHIFFMANN, R
    HILL, SC
    BRADY, RO
    ANNALS OF INTERNAL MEDICINE, 1995, 122 (01) : 33 - 39
  • [2] Hepatic response to enzyme replacement therapy (ERT) with mannose-terminated glucocerebrosidase in type 1 Gaucher disease.
    Malhotra, A
    Boxer, M
    Mistry, PK
    HEPATOLOGY, 2004, 40 (04) : 234A - 234A
  • [3] GAUCHER DISEASE TYPE-1 - SAFETY AND EFFICACY OF MACROPHAGE-TARGETED RECOMBINANT GLUCOCEREBROSIDASE THERAPY
    GRABOWSKI, GA
    PASTORES, G
    BRADY, RO
    BARTON, N
    CLINICAL RESEARCH, 1993, 41 (02): : A390 - A390
  • [4] Hepatic response to placental mannose-terminated glucocerebrosidase (alglucerase) in type 1 Gaucher disease (GD): The determinants of variable responsiveness
    Mistry, PK
    Butler, P
    Elstein, D
    Zimran, A
    HEPATOLOGY, 1997, 26 (04) : 275 - 275
  • [5] Velaglucerase alfa, a human recombinant glucocerebrosidase enzyme replacement therapy for type 1 Gaucher disease
    Pastores, Gregory M.
    CURRENT OPINION IN INVESTIGATIONAL DRUGS, 2010, 11 (04) : 472 - 478
  • [6] ENZYME REPLACEMENT THERAPY IN GAUCHER DISEASE TYPE-1
    AGGIO, MC
    FERNANDEZ, V
    MARCILESE, M
    MEDICINA-BUENOS AIRES, 1994, 54 (02) : 140 - 144
  • [7] Effect of mannose chain length on targeting of glucocerebrosidase for enzyme replacement therapy of Gaucher disease
    Van Patten, Scott M.
    Hughes, Heather
    Huff, Michael R.
    Piepenhagen, Peter A.
    Waire, James
    Qiu, Huawei
    Ganesa, Chandrashekar
    Reczek, David
    Ward, Paul V.
    Kutzko, Joseph P.
    Edmunds, Tim
    GLYCOBIOLOGY, 2007, 17 (05) : 467 - 478
  • [8] DEFICIENT ACTIVITY OF GLUCOCEREBROSIDASE IN URINE FROM PATIENTS WITH TYPE-1 GAUCHER DISEASE
    AERTS, JMFG
    DONKERKOOPMAN, WE
    KOOT, M
    BARRANGER, JA
    TAGER, JM
    SCHRAM, AW
    CLINICA CHIMICA ACTA, 1986, 158 (02) : 155 - 163
  • [9] GAUCHER DISEASE - COMPARATIVE-STUDY OF ACID-PHOSPHATASE AND GLUCOCEREBROSIDASE IN NORMAL AND TYPE-1 GAUCHER TISSUES
    CHOY, FYM
    AMERICAN JOURNAL OF MEDICAL GENETICS, 1985, 21 (03): : 519 - 528
  • [10] ENZYME AUGMENTATION THERAPY IN GAUCHER DISEASE TYPE-1 - DOSAGE EFFICACY AND ADVERSE-EFFECTS
    PASTORES, GM
    SIBILLE, AR
    GRABOWSKI, GA
    CLINICAL RESEARCH, 1992, 40 (02): : A357 - A357